Hi Angeliki, We know that for individuals with nonsense and other rare mutations, and those who love them, treatments cannot come soon enough. The CF Foundation is committed to finding effective treatments for the underlying cause of the disease for all people with CF, including those who are not eligible for or unable to tolerate CFTR modulators. We are funding research into several different genetic therapy strategies that could work for any person with CF, regardless of their CFTR mutations. You can learn more about these strategies at cff.org/GeneticTherapies, and see a list of the programs in development on the Drug Development Pipeline: cff.org/trials/pipeline
Hi, We know that for individuals with nonsense and other rare mutations, and those who love them, treatments cannot come soon enough. The CF Foundation is committed to finding effective treatments for the underlying cause of the disease for all people with CF, including those who are not eligible for or unable to tolerate CFTR modulators. We are funding research into several different genetic therapy strategies that could work for any person with CF, regardless of their CFTR mutations. You can learn more about these strategies at cff.org/GeneticTherapies, and see a list of the programs in development on the Drug Development Pipeline: cff.org/trials/pipeline
When will we have drug medicine for rare mutations cystic fibrosis?
Hi Angeliki,
We know that for individuals with nonsense and other rare mutations, and those who love them, treatments cannot come soon enough. The CF Foundation is committed to finding effective treatments for the underlying cause of the disease for all people with CF, including those who are not eligible for or unable to tolerate CFTR modulators. We are funding research into several different genetic therapy strategies that could work for any person with CF, regardless of their CFTR mutations. You can learn more about these strategies at cff.org/GeneticTherapies, and see a list of the programs in development on the Drug Development Pipeline: cff.org/trials/pipeline
Hi,
We know that for individuals with nonsense and other rare mutations, and those who love them, treatments cannot come soon enough. The CF Foundation is committed to finding effective treatments for the underlying cause of the disease for all people with CF, including those who are not eligible for or unable to tolerate CFTR modulators. We are funding research into several different genetic therapy strategies that could work for any person with CF, regardless of their CFTR mutations. You can learn more about these strategies at cff.org/GeneticTherapies, and see a list of the programs in development on the Drug Development Pipeline: cff.org/trials/pipeline