Gene Therapy and Sickle Cell Disease

Sickle cell disease is an inherited blood disorder that causes red blood cells to deform and become sickle (or crescent) shaped. Gene therapy and gene editing may offer a one-time treatment that addresses the genetic cause of sickle cell disease.
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[@Abhindas-s]

i really wish this can be really very helpful and affordable for people who with sickle cell

[@YoungHaveNot]

Crispr

[@navinsawesomeanddivineacco4221]

I just wanted to say, i love your Videos. Thank you so much for making them.

[@Ironman-BB]

Fact is this therapy is expensive and has complications using chemotherapy is not so easy it can damage so much that sometimes patients can get serious health issues or death. What's the success rate no one knows.
I am a SCD patient, last reporte is 76%S, 5%A and 15%F hemoglobin what should hope? Can I'm ever able to cure with this therapy and live normal life?

[@iwantcheesecake63]

Yea it's expensive but one time thing if done at embryonic stage. My sister got it done and I hope this becomes common and affordable in future. Many ppl don't even know about this.

[@eghoghoonosomiosesiamhe9518]

​@@iwantcheesecake63Hi, please are you saying your sister was cured of her SCD with gene therapy when she was still an embryo inutero? If so I'm really interested in this

[@arpanahaldar6351]

My 2 years old nephew have Wilson desease .can it will possible to become a normal child ...can he treat by this therapy ..plz help us...

[@user-dz1bh2di8q]

Dr Osade on RUclips has the best remedy for sickle cell ❤❤❤❤❤❤❤❤

[@mastermind1099]

Use lead/plumbum homeopathic dilution medicines for these type of problems.