Hello i from Slovakia and have a question for u my aunt have 14 years and doctors diagnoze him CMT4G type RUSSE at 6 years thay make the generic tests . My question is if this medication Can help him . And second question is how the illnes will continue i want to know if it is posible he Can end Up on wheelchair . Thanks for every information .
Dear, I am 21 year aged I am hearing form the age of 15 please do something because I can see how my life is ruin after few year I will be unable to walk.
Determining how long a drug development program will take to become an approved drug is challenging because each program is unique and it's unpredictable if a drug will meet the necessary milestones for approval. CMTRF currently has 5 CMT projects that have resulted in drug candidates that are now moving towards clinical trials and we aim to continue to fund more projects to increase the chances of getting approved treatments for CMT. If you would like to stay updated on the progress of these projects, please visit cmtrf.org/ and sign up for our email mailing list.
Genetic medicines have the potential to stop or even reverse the progression of diseases because they target the underlying genetic cause. This makes them promising therapeutic approaches to explore for CMT. As of today, CMTRF has funded 11 projects that explore various genetic technologies for CMT. To date, these projects have resulted in 3 genetic-based drug candidates that are now moving forward towards human clinical trials. For more information on genetic medicines and to stay up to date on all the CMT genetic-based therapy projects we fund, please visit cmtrf.org/gene-therapy/
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I wish these trials were offered in Canada
Hello i from Slovakia and have a question for u my aunt have 14 years and doctors diagnoze him CMT4G type RUSSE at 6 years thay make the generic tests . My question is if this medication Can help him . And second question is how the illnes will continue i want to know if it is posible he Can end Up on wheelchair . Thanks for every information .
Dear, I am 21 year aged I am hearing form the age of 15 please do something because I can see how my life is ruin after few year I will be unable to walk.
How much time it will take I am I am hearing it from the age of 15 and now I am 21 can you please tell me ?
Determining how long a drug development program will take to become an approved drug is challenging because each program is unique and it's unpredictable if a drug will meet the necessary milestones for approval. CMTRF currently has 5 CMT projects that have resulted in drug candidates that are now moving towards clinical trials and we aim to continue to fund more projects to increase the chances of getting approved treatments for CMT. If you would like to stay updated on the progress of these projects, please visit cmtrf.org/ and sign up for our email mailing list.
can gene therapy stop the progression of cmt?😂
Genetic medicines have the potential to stop or even reverse the progression of diseases because they target the underlying genetic cause. This makes them promising therapeutic approaches to explore for CMT. As of today, CMTRF has funded 11 projects that explore various genetic technologies for CMT. To date, these projects have resulted in 3 genetic-based drug candidates that are now moving forward towards human clinical trials. For more information on genetic medicines and to stay up to date on all the CMT genetic-based therapy projects we fund, please visit cmtrf.org/gene-therapy/
@@cmtresearchfoundation will these projects also be able applicable to hnpp?